GEMMABio is a therapeutics company focused on accelerating research and global access to life-changing advanced therapies for individuals with rare diseases. The company conducts research and product development to rapidly and affordably move gene therapy discoveries from the lab to patient treatment. Led by gene therapy industry pioneer Jim Wilson and an expert team whose members previously conducted work in academia, GEMMABio's mission is to develop novel gene therapies and ensure access for patients worldwide. The experts at the company have played a pivotal role in the field of genetic medicines for decades, driving advancements in AAV-based therapies.